Gene therapy is a revolutionary medical technique. It aims to treat or prevent diseases by altering genes. This approach can address genetic disorders and some cancers. It involves delivering healthy genes into a patient's cells. The potential benefits are significant. However, ethical concerns and regulatory challenges exist. Ongoing research is crucial for safe and effective applications. The future of gene therapy is promising.
On 23 April 2026, the United States Food and Drug Administration approved Otarmeni (lunsotogene parvec-cwha), the first dual adeno-associated virus vector-based gene therapy for inherited hearing loss. The...
